Our Focus

We are a clinical-stage biopharmaceutical company leveraging our proprietary non-viral gene engineering technologies to create ground-breaking, life-saving cell and gene therapies.

Our broad genetic engineering platform technologies are advancing potentially better and safer treatments to patients with serious diseases — blood cancers like multiple myeloma, solid tumor cancers like breast and ovarian cancer, and rare genetic diseases in the liver.

The organization is comprised of passionate, innovative, and nimble, results-oriented people driven by science to develop better options for patients with cancer and genetic diseases.